MLD Gene Therapy Approved in Europe
MLD gene therapy approved in the EU
MLD Gene Therapy Approved in Europe Read More »
Libmeldy
We’re thankful – even in 2020!
We heard earlier this week that nearly 4 in 5 people are already looking forward to putting 2020 behind us. The pandemic (family safety, work, school, loss of loved ones, individual and community response, social isolation, etc.), US elections, income, health, … it is affected every one of us, and it’s overwhelming. But we are
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Gene Therapy Recommended for Full EU EC Marketing Authorization Review
Gene therapy for early-onset MLD patients passed a huge milestone yesterday when the European Medicines Agency (EMA) Committee for Medicinal Products for Human Use (CHMP) adopted a positive opinion recommending full, or standard, marketing authorization for Libmeldy, by the European Commission (EC), which has the authority to grant marketing authorization for Libmeldy* in the European
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